pediatric rare anemia
Showing 1 - 25 of >10,000
Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
Not yet recruiting
- Sickle Cell Disease
- Interview
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Mar 30, 2023
Immune Thrombocytopenia, Autoimmune Hemolytic Anemia, Evans Syndrome Trial in France (data collection)
Recruiting
- Immune Thrombocytopenia
- +2 more
- data collection
-
Amiens, France
- +8 more
Jul 7, 2023
Marfan Syndrome and Quality of Life of Pediatric Patients
Recruiting
- Rare Diseases
- Pediatric Disorder
- Questionnaire
-
San Donato Milanese, Lombardia, ItalyIRCCS Policlinico San Donato
Feb 24, 2023
Hemoglobinopathies and Rare Inherited Anemia and Covid 19
Recruiting
- Haemoglobinopathies
-
Genova, Italy
- +1 more
May 4, 2022
Bone in Pediatric Gaucher Disease Related to Bone Pathology in
Recruiting
- Gaucher Disease
- Bone Diseases
-
Fairfax, VirginiaLysosomal and Rare disorder research and treatment center
Nov 6, 2023
Anemia of Chronic Kidney Disease Trial in Hackensack (vadadustat)
Suspended
- Anemia of Chronic Kidney Disease
-
Hackensack, New JerseyResearch Site
Aug 23, 2022
Anemia of Chronic Kidney Disease Trial in Hackensack (Vadadustat)
Suspended
- Anemia of Chronic Kidney Disease
-
Hackensack, New JerseyResearch Site
Aug 23, 2022
Immune Thrombocytopenia, Autoimmune Hemolytic Anemia, Evans Syndrome Trial in Graz (potential biomarkers)
Recruiting
- Immune Thrombocytopenia
- +3 more
- potential biomarkers
-
Graz, Styria, AustriaPediatric Hematology-Oncology Outpatient Clinic
Sep 8, 2022
Rare Diseases Trial in Hamburg
Completed
- Rare Diseases
-
Hamburg, GermanyUniversity Medical Center Hamburg-Eppendorf
Nov 27, 2021
Chronic Kidney Disease, Renal Anemia Trial (Roxadustat)
Not yet recruiting
- Chronic Kidney Disease
- Renal Anemia
- (no location specified)
Jul 25, 2023
Idiopathic Aplastic Anemia, Severe Aplastic Anemia, Moderate Aplastic Anemia Requiring Transfusions Trial (HSCT Arm group)
Not yet recruiting
- Idiopathic Aplastic Anemia
- +2 more
- HSCT Arm group
- (no location specified)
Jun 10, 2022
Bardet-Biedl Syndrome, POMC Deficiency Obesity, PCSK1 Deficiency Obesity Trial in Worldwide (Setmelanotide)
Active, not recruiting
- Bardet-Biedl Syndrome
- +3 more
-
Aurora, Colorado
- +5 more
Jul 21, 2022
Iron Deficiency Anemia Trial in Miami Springs, Miami (Ferric carboxymaltose)
Completed
- Iron Deficiency Anemia
- Ferric carboxymaltose
-
Miami Springs, Florida
- +1 more
Mar 17, 2022
Paroxysmal Nocturnal Hemoglobinuria Trial run by the Aplastic Anemia and MDS International Foundation
Recruiting
- Paroxysmal Nocturnal Hemoglobinuria
-
Bethesda, MarylandAplastic Anemia and MDS International Foundation
Feb 23, 2023
Non-adherence in Adults With Rare Disease
Withdrawn
- Cystic Fibrosis
- +5 more
- MAR-Scale
- (no location specified)
May 7, 2022
Iron Deficiency Anemia Trial in Waltham (Ferumoxytol)
Terminated
- Iron Deficiency Anemia
-
Waltham, MassachusettsAMAG Pharmaceuticals, Inc.
Mar 31, 2022
Iron Deficiency Anemia Trial in Waltham (Ferumoxytol, Oral Iron)
Terminated
- Iron Deficiency Anemia
- Ferumoxytol
- Oral Iron
-
Waltham, MassachusettsAMAG Pharmaceuticals, Inc.
Mar 31, 2022
Sickle Cell Anemia in Children Trial in Kampala (Hydroxyurea)
Active, not recruiting
- Sickle Cell Anemia in Children
-
Kampala, UgandaGlobal Health Uganda
May 11, 2022
Anemia Associated With Chronic Kidney Disease Trial in United States (Roxadustat)
Withdrawn
- Anemia Associated With Chronic Kidney Disease
-
Chicago, Illinois
- +3 more
Jun 29, 2022
Growth, Infant Development, Complementary Feeding Trial in Zonguldak (Baby-Led Weaning (BLW), Traditional Complementary Feeding
Completed
- Growth
- +5 more
- Baby-Led Weaning (BLW)
- Traditional Complementary Feeding (TCF)
-
Zonguldak, TurkeyZonguldakBEU
Mar 4, 2023
Iron Deficiency Anemia Trial in United States (Ferric carboxymaltose, Ferrous Sulfate)
Completed
- Iron Deficiency Anemia
- Ferric carboxymaltose
- Ferrous Sulfate
-
Little Rock, Arkansas
- +15 more
May 26, 2022
A Non-Interventional Post-Authorization Study of Carbaglu for
Enrolling by invitation
- Hyperammonemia
- +2 more
- carglumic acid
-
Indianapolis, IndianaRiley Children's Hospital
Apr 24, 2023